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Increased Transplant Related Mortality and Poor Donor Cell Chimerism in African American Children Undergoing Umbilical Cord Blood Transplantation. Institutional Experience at Lurie Children's Hospital of Chicago

Track: Poster Abstracts
Saturday, March 1, 2014, 6:45 PM-7:45 PM
Longhorn Hall E (Exhibit Level 1) (Gaylord Texan)
Mehboob Merchant, MBBS, SLS (ASCP) , Mathews' Center for Cellular Therapy, Northwestern Memorial Hospital, Chicago, IL
Reggie E Duerst, MD , Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, IL
Alfred Rademaker, Ph.D , Biostatistics Collaboration Center, Northwestern University Feinberg School of Medicine, Chicago, IL
Morris Kletzel, MD, FAAP, MBA , Pediatrics, Northwestern University Feinberg School of Medicine, Chicago, IL

 

We retrospectively evaluated all CBT to see if there is a correlation between patient ethnicity & transplant outcomes.  

Between 1/1995 & 1/2011 we performed 145 CBT for the treatment of malignant (95), non-malignant (50) conditions. Conditioning regimen: TBI + VP16 + Cy (79); TBI + TT + VP16 + Cy (16); Bu ± Cy ± FLUD (31); Cy ± TT or VP16 (12); other combinations (20). 

Malignancies: ALL (47), AML (29), other (19); Pt status: PR (7), CR1 (39), CR2 (42), CR3 (7).

Non-malignancies: Immunodeficiency (22); BM failure (10); Metabolic (6); Histiocytic (6); Hemoglobinopathy (6).

Cohort was 65 F, 80 M; median age 3.8 yr (0.1 - 20.6), wt 15.5 kg (3.0 - 73.0).

Ethnicity: Caucasian (52), Hispanic (44), African American (31), Asian (13), Mid Eastern (5). 

HLA match: 6/6 (15), 5/6 (38), 4/6 (83), 3/6 (9).

Median cell dose/Kg: 0.64^8 TNC, 0.56^8 MNC & 0.70^6 CD34. 

GvHD prophylaxis: MTX + ATG + CSA/FK506 ± PRED (92); MMF + ATG + CSA (16); CSA/FK506 + ATG ± PRED (37). 

Statistical analyses were done using Fisher's Exact and log-rank tests, column stats, and T- test. Significance was determined at p-value of 0.05.  

Overall Outcomes:

ANC >500 cells/µL was achieved in 70.3% of pts at 23 days (1 - 60); 66.2% achieved PLT count of >20,000 at 42 days (14 - 100); and 64.8% achieved >95% chimerism at 28 days (13 - 99). 100- day TRM was 22%. 84 pts (58%) are survivors. EFS > 1, 3 & 5 yr was 50%, 41% & 37% respectively, OS was 60%, 48% & 43%. 34 pts (23%) are event free for > 10 yr. Median follow up was 2.6 yr (1.2 - 16.4 yr). Grade II- IV acute GVHD was seen in 66 pts (46%), chronic GVHD in 8 (6%).

 

Table 1: Group Variables.

Variable

African American (31)

All Others (114)

P-value

Median

Range

Median

Range

Age 

4.0

0.2- 20.6

3.6

0.1- 17.4

0.11

TNC/Kg^8

0.54

0.05- 2.75

0.68

0.12- 4.27

0.19

MNC/Kg ^8

0.44

0.04- 2.55

0.57

0.08- 3.84

0.23

CD34/Kg^6

0.60

0.02- 7.6

0.80

0.02- 8.7

0.80

N=

%

N=

%

HLA 3/6, 4/6, 5/6, 6/6

4, 19, 6, 2

13, 61, 19, 7

5, 64, 32, 13

4, 56, 28, 11

0.18

Malignancy: Non-Malignancy

21, 10

67.7, 32.3

74, 40

64.9, 35.1

0.83

TBI: No TBI

24, 7

77.4, 22.6

71, 43

62.3, 37.7

0.14

 

 Table 2: Group Outcomes.

Outcomes

African American (31)

All Others (114)

P-value

Median

R=

Median

R=

Days to ANC

28

1- 51

23

15- 60

0.31

Days to PLT Engraft

45 

25-81 

42 

14- 105 

0.93 

Days to Chimerism

28

19- 97

29

13- 100

0.67

N=

%

N=

%

Alive, Died

17, 14

54.8, 45.2

67, 47

58.8, 41.2

0.69

Relapse

1 of 31

4.8

16 of 64

21.6

0.11

aGVHD

11

35.5

55

48.2

0.23

cGVHD

 6.4

 5.3

0.68

ANC Engraft

20

64.5

82

71.9

0.51

PLT Engraft

17 

 54.8

79 

 69.3

0.14

Chimerism >95%

15

48.4

79

69.3

0.031

TRM

12

38.7

20

17.5

0.012

Graph 1: K-M Survival.

 

 

Conclusion:

Children of African American ethnicity had statistically significant increased Transplant Related Mortality and showed poor chimerism compared to other groups. There was no other statistical significance between the two groups with respect to age, diagnosis, HLA match, cell dose, conditioning, survival, relapse, engraftment or GVHD. Also, there was no difference in transplant outcomes of the other individual ethnic groups.

Disclosures:
Nothing To Disclose